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Gene Therapy

Clinical Trials Cell Therapy Drug Development Viral Vectors Clinical Research Research Funding mRNA Technology Base Editing CRISPR Technology Adeno-Associated Virus

LEO Pharma to Acquire Replay in $50 Million Gene-Therapy Deal

The move underscores LEO’s effort to show a growth path ahead of a potential stock-market listing.

UCSF-Led Study Engineers CAR-T Cells In Vivo, Clearing Tumors in Mice

FDA Demands Placebo-Controlled Trial for UniQure’s Huntington’s Gene Therapy

FDA Proposes ‘Plausible Mechanism’ Pathway for Individualized Rare-Disease Therapies

Lilly Licenses MeiraGTx Eye Gene Therapy in Deal Worth Up to $475 Million

Altman’s Merge Labs Reportedly Recruits Caltech’s Mikhail Shapiro for Noninvasive Brain Interface

Lilly to Buy Adverum in Gene‑Therapy Deal Worth Up to $12.47 a Share

Retinal Implant and Camera Glasses Restore Central Vision in Advanced AMD, Study Finds

India Unveils First Homegrown Antibiotic Nafithromycin

FDA Names First 9 Drugs for ‘National Priority’ Fast-Track Reviews, Targeting 1–2-Month Decisions

Bristol Myers Squibb Buys Orbital Therapeutics for $1.5 Billion to Push In Vivo CAR‑T Into Autoimmune Care

Former FDA Biologics Chief Peter Marks Joins Eli Lilly to Lead Infectious Disease and Molecule Discovery

Gene Therapy Slows Huntington’s Progression by 75% in Early Trial, uniQure Says

Capsida Halts STXBP1 Gene Therapy Trial After First Pediatric Participant Dies

Kriya Nets $320 Million Series D as Odyssey Raises $213 Million and Amgen Retools Research Leadership

FDA Reinstates Biologics Director Vinay Prasad Less Than Two Weeks After Resignation

Single Birth Injection Protects Primates From HIV, Paves Way for Newborn Safety Trials

Precision RNA Therapy Reverses Progeria in Preclinical Models

Eli Lilly to Acquire Verve Therapeutics for $1.3 Billion

mRNA Nanoparticles Reverse HIV Latency in Resting T Cells