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EMA Panel Recommends Redemplo for Familial Chylomicronaemia Syndrome

The European Commission now reviews the application for an EU-wide licence.

Overview

  • EMA’s human medicines committee issued a positive opinion recommending EU marketing authorisation for Redemplo, also known as plozasiran.
  • Regulators cited a phase 3 trial in 75 adults that cut triglycerides by about 80% versus 17% with placebo and showed fewer acute pancreatitis events.
  • Plozasiran lowers triglycerides by blocking APOC3 production in the liver, which speeds the breakdown and clearance of fat from the blood.
  • The medicine comes as a 25 mg pre-filled syringe and is injected under the skin every three months as an add-on to a low-fat diet.
  • If the Commission grants approval, each country will decide price and coverage, and doctors can prescribe without genetic proof of FCS, which could widen access.